Therapeutic targeting of a microRNA to treat Duchenne muscular syatrophy

Anders M Naar (Inventor), Sakari Kauppinen (Inventor), Andreas Petri (Inventor)

Research output: Patent

Abstract

Methods of treating Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD), comprising administering an inhibitory nucleic acid that targets miR-128.

Original languageEnglish
IPCC12N 15/ 113 A I
Patent numberWO2018080658
Filing date03/05/2018
Country/TerritoryDenmark
Priority date23/06/2017
Priority numberUS201762523923P
Publication statusPublished - 2018

Cite this