Abstract
Methods of treating Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD), comprising administering an inhibitory nucleic acid that targets miR-128.
Original language | English |
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IPC | C12N 15/ 113 A I |
Patent number | WO2018080658 |
Filing date | 03/05/2018 |
Country/Territory | Denmark |
Priority date | 23/06/2017 |
Priority number | US201762523923P |
Publication status | Published - 2018 |